Amicus Therapeutics is a US-based biopharmaceutical company specializing in rare genetic diseases. The focus is on the development of therapies for lysosomal storage diseases such as Fabry's disease and Pompe disease. The aim is to offer innovative treatment options that go beyond the enzyme replacement therapies available to date.

Chiesi is an international pharmaceutical company headquartered in Parma, Italy. It develops and markets medicines in the fields of respiratory diseases, neonatology, transplant medicine and rare diseases. The company attaches great importance to research, sustainability and patient-oriented therapies.

Sanofi is a global healthcare company headquartered in Paris. It develops medicines and vaccines in areas such as rare diseases, immunology, oncology, diabetes and vaccines. Sanofi combines research and modern biotechnology to bring innovative therapies to people around the world.

Sciensus is a European healthcare company with a focus on specialized pharmaceutical care and patient care at home. It supports people with chronic and rare diseases by providing therapies, coordinating treatment pathways and facilitating access to innovative medicines.

Takeda is a global, research-driven pharmaceutical company headquartered in Japan. It focuses on rare diseases, oncology, gastroenterology, immunology and neuroscience. Takeda aims to improve the quality of life of patients worldwide through innovative therapies.